PMID36709920

Balakrishnan, B., Altassan, R., Budhraja, R., Liou, W., Lupo, A., Bryant, S., Mankouski, A., Radenkovic, S., Preston, G. J., Pandey, A., Boudina, S., Kozicz, T., Morava-Kozicz, E., Lai, K. (2023). AAV-based gene therapy prevents and halts the progression of dilated cardiomyopathy in a mouse model of phosphoglucomutase 1 deficiency (PGM1-CDG) Translational Research. S1931-5244(23)00004-X. [PubMed]